"Spinal muscular atrophy (SMA) is a progressive neurodegenerative disorder set in motion before birth."https://www.stjude.org/media-resources/news-releases/2025-medicine-science-news/promising-results-from-first-prenatal-therapy-for-spinal-muscular-atrophy.html?utm_source=join1440&utm_medium=email&utm_placement=newsletter&user_id=66c4c92f5d78644b3ac5d5b4
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